Repositorio Dspace

Listar por autor "Calandra, Cristian R."

Listar por autor "Calandra, Cristian R."

Ordenar por:Orden:Resultados:

  • Eplontersen for Hereditary Transthyretin Amyloidosis With Polyneuropathy 
    Coelho, Teresa; Marques, Wilson; Dasgupta, Noel R.; Chao, Chi-Chao; Parman, Yesim; Cavalcante França Jr, Marcondes; Guo, Yuh-Cherng; Wixner, Jonas; Ro, Long-Sun; Calandra, Cristian R.; Kowacs, Pedro A.; Berk, John L.; Obici, Laura; Barroso, Fabio Adrián; Weiler, Markus; Conceição, Isabel; Jung, Shiangtung W.; Buchele, Gustavo; Brambatti, Michela; NEURO-TTRansform Investigators (American Medical Association, 2023-09-28)
    Importance: Transthyretin gene silencing is an emerging treatment strategy for hereditary transthyretin (ATTRv) amyloidosis. Objective: To evaluate eplontersen, an investigational ligand-conjugated antisense oligonucleotide, ...
  • Practice guideline for the treatment of familial amyloid polyneuropathy 
    Carretero, Marcelina; Sáez, María S.; Posadas Martínez, María L.; Aguirre, María A.; Sorroche, Patricia; Negro, Agustina; Calandra, Cristian R.; Salutto, Valeria; Lautre, Andrea Rosana; Conti, Eugenia; León Cejas, Luciana; Reisin, Ricardo C.; Nucifora, Elsa M.; Rugiero, Marcelo (Fundación Revista Medicina (Buenos Aires), 2022)
    This clinical practice guideline for the treatment of familial amyloid polyneuropathy is based on the best available evidence of clinical effectiveness. A list of questions was generated with a PICO format focused on the ...